副腎白質ジストロフィーは、多くの場合男性に起こる障害で、主に神経系と副腎に影響を及ぼします。副腎とは、各腎臓の上にある小さな腺です。無βリポタンパク血症は、副腎白質ジストロフィー（副腎脊髄ニューロパシー/X連鎖副腎白質ジストロフィー）の一種であり、バッセン・コーンツヴァイク症候群とも呼ばれ、腸から食物脂肪を完全に吸収できないという、家族内発症する希少疾患です。この疾患は、リポタンパク質をつくるよう体に命令する遺伝子の欠陥に起因しています。時間とともに、脊柱の湾曲、筋力低下、視力低下などの症状が現れます。治療には脂溶性ビタミンを含有しているビタミン剤を大量に用います。
目次
Table of Contents
List of Tables
List of Figures
Introduction
Global Markets Direct Report Coverage
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Overview
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Therapeutics Development
Pipeline Overview
Pipeline by Companies
Pipeline by Universities/Institutes
Products under Development by Companies
Products under Development by Universities/Institutes
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Therapeutics Assessment
Assessment by Target
Assessment by Mechanism of Action
Assessment by Route of Administration
Assessment by Molecule Type
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Companies Involved in Therapeutics Development
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Drug Profiles
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Dormant Projects
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Discontinued Products
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Product Development Milestones
Featured News & Press Releases
Appendix
Methodology
Coverage
Secondary Research
Primary Research
Expert Panel Validation
Contact Us
Disclaimer
List of Tables
Number of Products under Development for Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)), 2022
Number of Products under Development by Companies, 2022
Number of Products under Development by Universities/Institutes, 2022
Products under Development by Companies, 2022
Products under Development by Companies, 2022 (Contd..1)
Products under Development by Universities/Institutes, 2022
Number of Products by Stage and Target, 2022
Number of Products by Stage and Mechanism of Action, 2022
Number of Products by Stage and Route of Administration, 2022
Number of Products by Stage and Molecule Type, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Apteeus SAS, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Ashvattha Therapeutics LLC, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Autobahn Therapeutics Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by bluebird bio Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Celularity Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Imstem Biotechnology Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by MedDay SA, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Minoryx Therapeutics sl, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Orpheris Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Poxel SA, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by ReceptoPharm Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by SwanBio Therapeutics Ltd, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Vigil Neuroscience Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Pipeline by Viking Therapeutics Inc, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Dormant Projects, 2022
Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)) - Discontinued Products, 2022
List of Figures
Number of Products under Development for Adrenoleukodystrophy (X-Linked Adrenoleukodystrophy (X-ALD)), 2022
Number of Products under Development by Companies, 2022
Number of Products under Development by Universities/Institutes, 2022
Number of Products by Top 10 Targets, 2022
Number of Products by Stage and Top 10 Targets, 2022
Number of Products by Top 10 Mechanism of Actions, 2022
Number of Products by Stage and Top 10 Mechanism of Actions, 2022
Number of Products by Top 10 Routes of Administration, 2022
Number of Products by Stage and Top 10 Routes of Administration, 2022
Number of Products by Top 10 Molecule Types, 2022
Number of Products by Stage and Top 10 Molecule Types, 2022
