目次

Table of Contents

1 Executive Summary
1.1 Market overview
Exhibit 01: Executive Summary - Chart on Market Overview
Exhibit 02: Executive Summary - Data Table on Market Overview
Exhibit 03: Executive Summary - Chart on Global Market Characteristics
Exhibit 04: Executive Summary - Chart on Market By Geographical Landscape
Exhibit 05: Executive Summary - Chart on Market Segmentation by Distribution Channel
Exhibit 06: Executive Summary - Chart on Market Segmentation by Route of Administration
Exhibit 07: Executive Summary - Chart on Incremental Growth
Exhibit 08: Executive Summary - Data Table on Incremental Growth
Exhibit 09: Executive Summary - Chart on Vendor Market Positioning

2 Market Landscape
2.1 Market ecosystem
Exhibit 10: Parent market
Exhibit 11: Market Characteristics

3 Market Sizing
3.1 Market definition
Exhibit 12: Offerings of vendors included in the market definition
3.2 Market segment analysis
Exhibit 13: Market segments
3.3 Market size 2023
3.4 Market outlook: Forecast for 2023-2028
Exhibit 14: Chart on Global - Market size and forecast 2023-2028 ($ million)
Exhibit 15: Data Table on Global - Market size and forecast 2023-2028 ($ million)
Exhibit 16: Chart on Global Market: Year-over-year growth 2023-2028 (%)
Exhibit 17: Data Table on Global Market: Year-over-year growth 2023-2028 (%)

4 Historic Market Size
4.1 Global fabry disease drugs market 2018 - 2022
Exhibit 18: Historic Market Size - Data Table on global fabry disease drugs market 2018 - 2022 ($ million)
4.2 Distribution Channel Segment Analysis 2018 - 2022
Exhibit 19: Historic Market Size - Distribution Channel Segment 2018 - 2022 ($ million)
4.3 Route Of Administration Segment Analysis 2018 - 2022
Exhibit 20: Historic Market Size - Route Of Administration Segment 2018 - 2022 ($ million)
4.4 Geography Segment Analysis 2018 - 2022
Exhibit 21: Historic Market Size - Geography Segment 2018 - 2022 ($ million)
4.5 Country Segment Analysis 2018 - 2022
Exhibit 22: Historic Market Size - Country Segment 2018 - 2022 ($ million)

5 Five Forces Analysis
5.1 Five forces summary
Exhibit 23: Five forces analysis - Comparison between 2023 and 2028
5.2 Bargaining power of buyers
Exhibit 24: Chart on Bargaining power of buyers - Impact of key factors 2023 and 2028
5.3 Bargaining power of suppliers
Exhibit 25: Bargaining power of suppliers - Impact of key factors in 2023 and 2028
5.4 Threat of new entrants
Exhibit 26: Threat of new entrants - Impact of key factors in 2023 and 2028
5.5 Threat of substitutes
Exhibit 27: Threat of substitutes - Impact of key factors in 2023 and 2028
5.6 Threat of rivalry
Exhibit 28: Threat of rivalry - Impact of key factors in 2023 and 2028
5.7 Market condition
Exhibit 29: Chart on Market condition - Five forces 2023 and 2028

6 Market Segmentation by Distribution Channel
6.1 Market segments
Exhibit 30: Chart on Distribution Channel - Market share 2023-2028 (%)
Exhibit 31: Data Table on Distribution Channel - Market share 2023-2028 (%)
6.2 Comparison by Distribution Channel
Exhibit 32: Chart on Comparison by Distribution Channel
Exhibit 33: Data Table on Comparison by Distribution Channel
6.3 Hospital pharmacies - Market size and forecast 2023-2028
Exhibit 34: Chart on Hospital pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibit 35: Data Table on Hospital pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibit 36: Chart on Hospital pharmacies - Year-over-year growth 2023-2028 (%)
Exhibit 37: Data Table on Hospital pharmacies - Year-over-year growth 2023-2028 (%)
6.4 Retail pharmacies - Market size and forecast 2023-2028
Exhibit 38: Chart on Retail pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibit 39: Data Table on Retail pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibit 40: Chart on Retail pharmacies - Year-over-year growth 2023-2028 (%)
Exhibit 41: Data Table on Retail pharmacies - Year-over-year growth 2023-2028 (%)
6.5 Online pharmacies - Market size and forecast 2023-2028
Exhibit 42: Chart on Online pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibit 43: Data Table on Online pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibit 44: Chart on Online pharmacies - Year-over-year growth 2023-2028 (%)
Exhibit 45: Data Table on Online pharmacies - Year-over-year growth 2023-2028 (%)
6.6 Market opportunity by Distribution Channel
Exhibit 46: Market opportunity by Distribution Channel ($ million)
Exhibit 47: Data Table on Market opportunity by Distribution Channel ($ million)

7 Market Segmentation by Route of Administration
7.1 Market segments
Exhibit 48: Chart on Route of Administration - Market share 2023-2028 (%)
Exhibit 49: Data Table on Route of Administration - Market share 2023-2028 (%)
7.2 Comparison by Route of Administration
Exhibit 50: Chart on Comparison by Route of Administration
Exhibit 51: Data Table on Comparison by Route of Administration
7.3 Intravenous route - Market size and forecast 2023-2028
Exhibit 52: Chart on Intravenous route - Market size and forecast 2023-2028 ($ million)
Exhibit 53: Data Table on Intravenous route - Market size and forecast 2023-2028 ($ million)
Exhibit 54: Chart on Intravenous route - Year-over-year growth 2023-2028 (%)
Exhibit 55: Data Table on Intravenous route - Year-over-year growth 2023-2028 (%)
7.4 Oral route - Market size and forecast 2023-2028
Exhibit 56: Chart on Oral route - Market size and forecast 2023-2028 ($ million)
Exhibit 57: Data Table on Oral route - Market size and forecast 2023-2028 ($ million)
Exhibit 58: Chart on Oral route - Year-over-year growth 2023-2028 (%)
Exhibit 59: Data Table on Oral route - Year-over-year growth 2023-2028 (%)
7.5 Market opportunity by Route of Administration
Exhibit 60: Market opportunity by Route of Administration ($ million)
Exhibit 61: Data Table on Market opportunity by Route of Administration ($ million)

8 Customer Landscape
8.1 Customer landscape overview
Exhibit 62: Analysis of price sensitivity, lifecycle, customer purchase basket, adoption rates, and purchase criteria

9 Geographic Landscape
9.1 Geographic segmentation
Exhibit 63: Chart on Market share By Geographical Landscape 2023-2028 (%)
Exhibit 64: Data Table on Market share By Geographical Landscape 2023-2028 (%)
9.2 Geographic comparison
Exhibit 65: Chart on Geographic comparison
Exhibit 66: Data Table on Geographic comparison
9.3 North America - Market size and forecast 2023-2028
Exhibit 67: Chart on North America - Market size and forecast 2023-2028 ($ million)
Exhibit 68: Data Table on North America - Market size and forecast 2023-2028 ($ million)
Exhibit 69: Chart on North America - Year-over-year growth 2023-2028 (%)
Exhibit 70: Data Table on North America - Year-over-year growth 2023-2028 (%)
9.4 Europe - Market size and forecast 2023-2028
Exhibit 71: Chart on Europe - Market size and forecast 2023-2028 ($ million)
Exhibit 72: Data Table on Europe - Market size and forecast 2023-2028 ($ million)
Exhibit 73: Chart on Europe - Year-over-year growth 2023-2028 (%)
Exhibit 74: Data Table on Europe - Year-over-year growth 2023-2028 (%)
9.5 Asia - Market size and forecast 2023-2028
Exhibit 75: Chart on Asia - Market size and forecast 2023-2028 ($ million)
Exhibit 76: Data Table on Asia - Market size and forecast 2023-2028 ($ million)
Exhibit 77: Chart on Asia - Year-over-year growth 2023-2028 (%)
Exhibit 78: Data Table on Asia - Year-over-year growth 2023-2028 (%)
9.6 Rest of World (ROW) - Market size and forecast 2023-2028
Exhibit 79: Chart on Rest of World (ROW) - Market size and forecast 2023-2028 ($ million)
Exhibit 80: Data Table on Rest of World (ROW) - Market size and forecast 2023-2028 ($ million)
Exhibit 81: Chart on Rest of World (ROW) - Year-over-year growth 2023-2028 (%)
Exhibit 82: Data Table on Rest of World (ROW) - Year-over-year growth 2023-2028 (%)
9.7 US - Market size and forecast 2023-2028
Exhibit 83: Chart on US - Market size and forecast 2023-2028 ($ million)
Exhibit 84: Data Table on US - Market size and forecast 2023-2028 ($ million)
Exhibit 85: Chart on US - Year-over-year growth 2023-2028 (%)
Exhibit 86: Data Table on US - Year-over-year growth 2023-2028 (%)
9.8 China - Market size and forecast 2023-2028
Exhibit 87: Chart on China - Market size and forecast 2023-2028 ($ million)
Exhibit 88: Data Table on China - Market size and forecast 2023-2028 ($ million)
Exhibit 89: Chart on China - Year-over-year growth 2023-2028 (%)
Exhibit 90: Data Table on China - Year-over-year growth 2023-2028 (%)
9.9 Germany - Market size and forecast 2023-2028
Exhibit 91: Chart on Germany - Market size and forecast 2023-2028 ($ million)
Exhibit 92: Data Table on Germany - Market size and forecast 2023-2028 ($ million)
Exhibit 93: Chart on Germany - Year-over-year growth 2023-2028 (%)
Exhibit 94: Data Table on Germany - Year-over-year growth 2023-2028 (%)
9.10 UK - Market size and forecast 2023-2028
Exhibit 95: Chart on UK - Market size and forecast 2023-2028 ($ million)
Exhibit 96: Data Table on UK - Market size and forecast 2023-2028 ($ million)
Exhibit 97: Chart on UK - Year-over-year growth 2023-2028 (%)
Exhibit 98: Data Table on UK - Year-over-year growth 2023-2028 (%)
9.11 Japan - Market size and forecast 2023-2028
Exhibit 99: Chart on Japan - Market size and forecast 2023-2028 ($ million)
Exhibit 100: Data Table on Japan - Market size and forecast 2023-2028 ($ million)
Exhibit 101: Chart on Japan - Year-over-year growth 2023-2028 (%)
Exhibit 102: Data Table on Japan - Year-over-year growth 2023-2028 (%)
9.12 Market opportunity By Geographical Landscape
Exhibit 103: Market opportunity By Geographical Landscape ($ million)
Exhibit 104: Data Tables on Market opportunity By Geographical Landscape ($ million)

10 Drivers, Challenges, and Trends
10.1 Market drivers
10.2 Market challenges
10.3 Impact of drivers and challenges
Exhibit 105: Impact of drivers and challenges in 2023 and 2028
10.4 Market trends

11 Vendor Landscape
11.1 Overview
11.2 Vendor landscape
Exhibit 106: Overview on Criticality of inputs and Factors of differentiation
11.3 Landscape disruption
Exhibit 107: Overview on factors of disruption
11.4 Industry risks
Exhibit 108: Impact of key risks on business

12 Vendor Analysis
12.1 Vendors covered
Exhibit 109: Vendors covered
12.2 Market positioning of vendors
Exhibit 110: Matrix on vendor position and classification
12.3 4D Molecular Therapeutics Inc.
Exhibit 111: 4D Molecular Therapeutics Inc. - Overview
Exhibit 112: 4D Molecular Therapeutics Inc. - Product / Service
Exhibit 113: 4D Molecular Therapeutics Inc. - Key offerings
12.4 Amicus Therapeutics Inc.
Exhibit 114: Amicus Therapeutics Inc. - Overview
Exhibit 115: Amicus Therapeutics Inc. - Product / Service
Exhibit 116: Amicus Therapeutics Inc. - Key offerings
12.5 CHIESI Farmaceutici SpA
Exhibit 117: CHIESI Farmaceutici SpA - Overview
Exhibit 118: CHIESI Farmaceutici SpA - Product / Service
Exhibit 119: CHIESI Farmaceutici SpA - Key offerings
12.6 Freeline Therapeutics Holdings plc
Exhibit 120: Freeline Therapeutics Holdings plc - Overview
Exhibit 121: Freeline Therapeutics Holdings plc - Product / Service
Exhibit 122: Freeline Therapeutics Holdings plc - Key offerings
12.7 Idorsia Pharmaceuticals Ltd.
Exhibit 123: Idorsia Pharmaceuticals Ltd. - Overview
Exhibit 124: Idorsia Pharmaceuticals Ltd. - Product / Service
Exhibit 125: Idorsia Pharmaceuticals Ltd. - Key offerings
12.8 Sangamo Therapeutics Inc.
Exhibit 126: Sangamo Therapeutics Inc. - Overview
Exhibit 127: Sangamo Therapeutics Inc. - Product / Service
Exhibit 128: Sangamo Therapeutics Inc. - Key offerings
12.9 Sanofi SA
Exhibit 129: Sanofi SA - Overview
Exhibit 130: Sanofi SA - Business segments
Exhibit 131: Sanofi SA - Key news
Exhibit 132: Sanofi SA - Key offerings
Exhibit 133: Sanofi SA - Segment focus
12.10 Takeda Pharmaceutical Co. Ltd.
Exhibit 134: Takeda Pharmaceutical Co. Ltd. - Overview
Exhibit 135: Takeda Pharmaceutical Co. Ltd. - Product / Service
Exhibit 136: Takeda Pharmaceutical Co. Ltd. - Key news
Exhibit 137: Takeda Pharmaceutical Co. Ltd. - Key offerings

13 Appendix
13.1 Scope of the report
13.2 Inclusions and exclusions checklist
Exhibit 138: Inclusions checklist
Exhibit 139: Exclusions checklist
13.3 Currency conversion rates for US$
Exhibit 140: Currency conversion rates for US$
13.4 Research methodology
Exhibit 141: Research methodology
Exhibit 142: Validation techniques employed for market sizing
Exhibit 143: Information sources
13.5 List of abbreviations
Exhibit 144: List of abbreviations

Exhibits:
Exhibits1: Executive Summary - Chart on Market Overview
Exhibits2: Executive Summary - Data Table on Market Overview
Exhibits3: Executive Summary - Chart on Global Market Characteristics
Exhibits4: Executive Summary - Chart on Market By Geographical Landscape
Exhibits5: Executive Summary - Chart on Market Segmentation by Distribution Channel
Exhibits6: Executive Summary - Chart on Market Segmentation by Route of Administration
Exhibits7: Executive Summary - Chart on Incremental Growth
Exhibits8: Executive Summary - Data Table on Incremental Growth
Exhibits9: Executive Summary - Chart on Vendor Market Positioning
Exhibits10: Parent market
Exhibits11: Market Characteristics
Exhibits12: Offerings of vendors included in the market definition
Exhibits13: Market segments
Exhibits14: Chart on Global - Market size and forecast 2023-2028 ($ million)
Exhibits15: Data Table on Global - Market size and forecast 2023-2028 ($ million)
Exhibits16: Chart on Global Market: Year-over-year growth 2023-2028 (%)
Exhibits17: Data Table on Global Market: Year-over-year growth 2023-2028 (%)
Exhibits18: Five forces analysis - Comparison between 2023 and 2028
Exhibits19: Chart on Bargaining power of buyers - Impact of key factors 2023 and 2028
Exhibits20: Bargaining power of suppliers - Impact of key factors in 2023 and 2028
Exhibits21: Threat of new entrants - Impact of key factors in 2023 and 2028
Exhibits22: Threat of substitutes - Impact of key factors in 2023 and 2028
Exhibits23: Threat of rivalry - Impact of key factors in 2023 and 2028
Exhibits24: Chart on Market condition - Five forces 2023 and 2028
Exhibits25: Chart on Distribution Channel - Market share 2023-2028 (%)
Exhibits26: Data Table on Distribution Channel - Market share 2023-2028 (%)
Exhibits27: Chart on Comparison by Distribution Channel
Exhibits28: Data Table on Comparison by Distribution Channel
Exhibits29: Chart on Hospital pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibits30: Data Table on Hospital pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibits31: Chart on Hospital pharmacies - Year-over-year growth 2023-2028 (%)
Exhibits32: Data Table on Hospital pharmacies - Year-over-year growth 2023-2028 (%)
Exhibits33: Chart on Retail pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibits34: Data Table on Retail pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibits35: Chart on Retail pharmacies - Year-over-year growth 2023-2028 (%)
Exhibits36: Data Table on Retail pharmacies - Year-over-year growth 2023-2028 (%)
Exhibits37: Chart on Online pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibits38: Data Table on Online pharmacies - Market size and forecast 2023-2028 ($ million)
Exhibits39: Chart on Online pharmacies - Year-over-year growth 2023-2028 (%)
Exhibits40: Data Table on Online pharmacies - Year-over-year growth 2023-2028 (%)
Exhibits41: Market opportunity by Distribution Channel ($ million)
Exhibits42: Data Table on Market opportunity by Distribution Channel ($ million)
Exhibits43: Chart on Route of Administration - Market share 2023-2028 (%)
Exhibits44: Data Table on Route of Administration - Market share 2023-2028 (%)
Exhibits45: Chart on Comparison by Route of Administration
Exhibits46: Data Table on Comparison by Route of Administration
Exhibits47: Chart on Intravenous route - Market size and forecast 2023-2028 ($ million)
Exhibits48: Data Table on Intravenous route - Market size and forecast 2023-2028 ($ million)
Exhibits49: Chart on Intravenous route - Year-over-year growth 2023-2028 (%)
Exhibits50: Data Table on Intravenous route - Year-over-year growth 2023-2028 (%)
Exhibits51: Chart on Oral route - Market size and forecast 2023-2028 ($ million)
Exhibits52: Data Table on Oral route - Market size and forecast 2023-2028 ($ million)
Exhibits53: Chart on Oral route - Year-over-year growth 2023-2028 (%)
Exhibits54: Data Table on Oral route - Year-over-year growth 2023-2028 (%)
Exhibits55: Market opportunity by Route of Administration ($ million)
Exhibits56: Data Table on Market opportunity by Route of Administration ($ million)
Exhibits57: Analysis of price sensitivity, lifecycle, customer purchase basket, adoption rates, and purchase criteria
Exhibits58: Chart on Market share By Geographical Landscape 2023-2028 (%)
Exhibits59: Data Table on Market share By Geographical Landscape 2023-2028 (%)
Exhibits60: Chart on Geographic comparison
Exhibits61: Data Table on Geographic comparison
Exhibits62: Chart on North America - Market size and forecast 2023-2028 ($ million)
Exhibits63: Data Table on North America - Market size and forecast 2023-2028 ($ million)
Exhibits64: Chart on North America - Year-over-year growth 2023-2028 (%)
Exhibits65: Data Table on North America - Year-over-year growth 2023-2028 (%)
Exhibits66: Chart on Europe - Market size and forecast 2023-2028 ($ million)
Exhibits67: Data Table on Europe - Market size and forecast 2023-2028 ($ million)
Exhibits68: Chart on Europe - Year-over-year growth 2023-2028 (%)
Exhibits69: Data Table on Europe - Year-over-year growth 2023-2028 (%)
Exhibits70: Chart on Asia - Market size and forecast 2023-2028 ($ million)
Exhibits71: Data Table on Asia - Market size and forecast 2023-2028 ($ million)
Exhibits72: Chart on Asia - Year-over-year growth 2023-2028 (%)
Exhibits73: Data Table on Asia - Year-over-year growth 2023-2028 (%)
Exhibits74: Chart on Rest of World (ROW) - Market size and forecast 2023-2028 ($ million)
Exhibits75: Data Table on Rest of World (ROW) - Market size and forecast 2023-2028 ($ million)
Exhibits76: Chart on Rest of World (ROW) - Year-over-year growth 2023-2028 (%)
Exhibits77: Data Table on Rest of World (ROW) - Year-over-year growth 2023-2028 (%)
Exhibits78: Chart on US - Market size and forecast 2023-2028 ($ million)
Exhibits79: Data Table on US - Market size and forecast 2023-2028 ($ million)
Exhibits80: Chart on US - Year-over-year growth 2023-2028 (%)
Exhibits81: Data Table on US - Year-over-year growth 2023-2028 (%)
Exhibits82: Chart on China - Market size and forecast 2023-2028 ($ million)
Exhibits83: Data Table on China - Market size and forecast 2023-2028 ($ million)
Exhibits84: Chart on China - Year-over-year growth 2023-2028 (%)
Exhibits85: Data Table on China - Year-over-year growth 2023-2028 (%)
Exhibits86: Chart on Germany - Market size and forecast 2023-2028 ($ million)
Exhibits87: Data Table on Germany - Market size and forecast 2023-2028 ($ million)
Exhibits88: Chart on Germany - Year-over-year growth 2023-2028 (%)
Exhibits89: Data Table on Germany - Year-over-year growth 2023-2028 (%)
Exhibits90: Chart on UK - Market size and forecast 2023-2028 ($ million)
Exhibits91: Data Table on UK - Market size and forecast 2023-2028 ($ million)
Exhibits92: Chart on UK - Year-over-year growth 2023-2028 (%)
Exhibits93: Data Table on UK - Year-over-year growth 2023-2028 (%)
Exhibits94: Chart on Japan - Market size and forecast 2023-2028 ($ million)
Exhibits95: Data Table on Japan - Market size and forecast 2023-2028 ($ million)
Exhibits96: Chart on Japan - Year-over-year growth 2023-2028 (%)
Exhibits97: Data Table on Japan - Year-over-year growth 2023-2028 (%)
Exhibits98: Market opportunity By Geographical Landscape ($ million)
Exhibits99: Data Tables on Market opportunity By Geographical Landscape ($ million)
Exhibits100: Impact of drivers and challenges in 2023 and 2028
Exhibits101: Overview on Criticality of inputs and Factors of differentiation
Exhibits102: Overview on factors of disruption
Exhibits103: Impact of key risks on business
Exhibits104: Vendors covered
Exhibits105: Matrix on vendor position and classification
Exhibits106: 4D Molecular Therapeutics Inc. - Overview
Exhibits107: 4D Molecular Therapeutics Inc. - Product / Service
Exhibits108: 4D Molecular Therapeutics Inc. - Key offerings
Exhibits109: Amicus Therapeutics Inc. - Overview
Exhibits110: Amicus Therapeutics Inc. - Product / Service
Exhibits111: Amicus Therapeutics Inc. - Key offerings
Exhibits112: CHIESI Farmaceutici SpA - Overview
Exhibits113: CHIESI Farmaceutici SpA - Product / Service
Exhibits114: CHIESI Farmaceutici SpA - Key offerings
Exhibits115: Freeline Therapeutics Holdings plc - Overview
Exhibits116: Freeline Therapeutics Holdings plc - Product / Service
Exhibits117: Freeline Therapeutics Holdings plc - Key offerings
Exhibits118: Idorsia Pharmaceuticals Ltd. - Overview
Exhibits119: Idorsia Pharmaceuticals Ltd. - Product / Service
Exhibits120: Idorsia Pharmaceuticals Ltd. - Key offerings
Exhibits121: Sangamo Therapeutics Inc. - Overview
Exhibits122: Sangamo Therapeutics Inc. - Product / Service
Exhibits123: Sangamo Therapeutics Inc. - Key offerings
Exhibits124: Sanofi SA - Overview
Exhibits125: Sanofi SA - Business segments
Exhibits126: Sanofi SA - Key news
Exhibits127: Sanofi SA - Key offerings
Exhibits128: Sanofi SA - Segment focus
Exhibits129: Takeda Pharmaceutical Co. Ltd. - Overview
Exhibits130: Takeda Pharmaceutical Co. Ltd. - Product / Service
Exhibits131: Takeda Pharmaceutical Co. Ltd. - Key news
Exhibits132: Takeda Pharmaceutical Co. Ltd. - Key offerings
Exhibits133: Inclusions checklist
Exhibits134: Exclusions checklist
Exhibits135: Currency conversion rates for US$
Exhibits136: Research methodology
Exhibits137: Validation techniques employed for market sizing
Exhibits138: Information sources
Exhibits139: List of abbreviations