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嚢胞性線維症治療薬の世界市場洞察(2025年)- 2030年までの分析と予測(市場参加者別、地域別、技術別、用途別、製品タイプ別)

Prof Research

Cystic Fibrosis Therapeutics Global Market Insights 2025, Analysis and Forecast to 2030, by Market Participants, Regions, Technology, Application, Product Type

発刊日 2025/05/25

言語英語

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ライセンス/価格92ページ

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レポート概要

嚢胞性線維症治療薬市場の概要

導入と市場概要

嚢胞性線維症(CF)治療薬には、CFTR調節薬、膵酵素サプリメント、粘液溶解薬、気管支拡張薬などがあり、世界で約10万5,000人の患者(アメリカで4万人、ヨーロッパで5万人)が罹患している遺伝性疾患を治療します。市場は、新生児スクリーニングによる診断率の上昇と、F508del患者の90%で肺機能を改善し、入院を60%削減するTrikaftaなどの革新的なCFTR調節薬によって牽引されています。早期介入、患者の寿命延長(早期治療による生存率30%向上)、そしてOECD加盟国の60%がCFTR調節薬をカバーしている支援政策が需要を牽引しています。世界のCF治療薬市場は、2025年には60億〜100億米ドルに達すると推定され、2030年まで年平均成長率(CAGR)11%〜16%で成長します。

地域別市場動向

  • 北アメリカ:アメリカは新生児スクリーニングとトリカフタ(Trikafta)の普及でリードし、カナダはCFケアへのアクセスを重視しています。
  • ヨーロッパ:イギリス、ドイツ、フランスは、CFTR調節薬の強力な償還により成長を牽引しています。
  • アジア太平洋地域:オーストラリアはCFスクリーニングを拡大し、日本は新規治療法に注力しています。
  • その他の地域:ブラジルはCFケアのインフラ整備を進め、中東は遺伝子スクリーニングに取り組んでいます。

流通チャネル分析

  • 病院薬局:CFTR調節薬の処方箋増加に伴い、11.5%〜16.5%の成長が見込まれます。専門医療への注目が高まっています。
  • オンライン薬局:患者の利便性向上に伴い、12.0%〜17.0%の成長が見込まれます。デジタルアクセスの進化が注目されています。
  • 小売薬局:支持療法を含む、10.5%〜15.5%の成長が見込まれます。地域密着型医療への注目が高まっています。

タイプ分析

  • CFTR調節薬:12.0%〜17.0%の成長が見込まれ、革新的な成果が評価されています。トレンドはVanzaなどの3剤併用療法に焦点が当てられています。
  • 膵酵素サプリメント:10.5%〜15.5%の成長が見込まれ、消化に不可欠です。進歩は高効力製剤に重点を置いています。
  • 粘液溶解薬:10.0%〜15.0%の成長が見込まれ、気道クリアランスに使用されます。トレンドは吸入療法に重点を置いています。
  • 気管支拡張薬:9.5%〜14.5%の成長が見込まれ、症状緩和に適しています。開発は長時間作用型薬剤に重点を置いています。

主要市場プレーヤー

  • Vertex Pharmaceuticals:TrikaftaなどのCFTRモジュレーターを開発。
  • AbbVie:膵酵素サプリメントを開発。
  • Gilead:CF支持療法に注力。
  • Roche:気道管理用の粘液溶解薬を提供。
  • Sionna Therapeutics:CFTRに対する新たな治療法を開発。

ポーターのファイブフォース分析

  • 規参入の脅威:希少疾病用医薬品に対する研究開発費の高さと規制上の障壁のため、低いです。
  • 代替品の脅威:CFTR調節薬は独自の技術であるため、低いですが、遺伝子治療が将来的に競合となる可能性があります。
  • 買い手の交渉力:中程度です。保険会社が価格交渉を行いますが、代替品が限られているため、プロバイダーの競争力は高いです。
  • サプライヤーの交渉力:低いです。APIメーカーは複数存在します。
  • 競合:中程度です。Vertexが市場を独占していますが、新興企業が革新的な治療法で挑戦してきます。

市場機会と課題

  • 機会
    ➣ 世界中で10万5,000人のCF患者に対応。
    ➣ CFTR調節薬を活用することで、F508del患者の90%の転帰を改善。
    ➣ 新生児スクリーニングの活用により、診断率を20%向上。
    ➣ 早期介入を支援し、生存率を30%向上。
    ➣ OECDの償還対象範囲の60%を活用。
    ➣ CFFによる660万米ドルの投資など、研究資金の拡大。
  • 課題
    ➣ CFTR調節薬の高コストがアクセスを制限。
    ➣ 新規治療法の規制の遅延。
    ➣ 発展途上地域におけるCFインフラの不足。
    ➣ 新興遺伝子治療との競争。
    ➣ 複雑なレジメンに対する患者の服薬遵守の問題。

レポート詳細

目次

Table of Contents

Chapter 1 Executive Summary

Chapter 2 Abbreviation and Acronyms

Chapter 3 Preface
3.1 Research Scope
3.2 Research Sources
3.2.1 Data Sources
3.2.2 Assumptions
3.3 Research Method

Chapter Four Market Landscape
4.1 Market Overview
4.2 Classification/Types
4.3 Application/End Users

Chapter 5 Market Trend Analysis
5.1 Introduction
5.2 Drivers
5.3 Restraints
5.4 Opportunities
5.5 Threats

Chapter 6 Industry Chain Analysis
6.1 Upstream/Suppliers Analysis
6.2 Cystic Fibrosis Therapeutics Analysis
6.2.1 Technology Analysis
6.2.2 Cost Analysis
6.2.3 Market Channel Analysis
6.3 Downstream Buyers/End Users

Chapter 7 Latest Market Dynamics
7.1 Latest News
7.2 Merger and Acquisition
7.3 Planned/Future Project
7.4 Policy Dynamics

Chapter 8 Historical and Forecast Cystic Fibrosis Therapeutics Market in North America (2020-2030)
8.1 Cystic Fibrosis Therapeutics Market Size
8.2 Cystic Fibrosis Therapeutics Market by End Use
8.3 Competition by Players/Suppliers
8.4 Cystic Fibrosis Therapeutics Market Size by Type
8.5 Key Countries Analysis
8.5.1 United States
8.5.2 Canada
8.5.3 Mexico

Chapter 9 Historical and Forecast Cystic Fibrosis Therapeutics Market in South America (2020-2030)
9.1 Cystic Fibrosis Therapeutics Market Size
9.2 Cystic Fibrosis Therapeutics Market by End Use
9.3 Competition by Players/Suppliers
9.4 Cystic Fibrosis Therapeutics Market Size by Type
9.5 Key Countries Analysis
9.5.1 Brazil
9.5.2 Argentina
9.5.3 Chile
9.5.4 Peru

Chapter 10 Historical and Forecast Cystic Fibrosis Therapeutics Market in Asia & Pacific (2020-2030)
10.1 Cystic Fibrosis Therapeutics Market Size
10.2 Cystic Fibrosis Therapeutics Market by End Use
10.3 Competition by Players/Suppliers
10.4 Cystic Fibrosis Therapeutics Market Size by Type
10.5 Key Countries Analysis
10.5.1 China
10.5.2 India
10.5.3 Japan
10.5.4 South Korea
10.5.5 Southest Asia
10.5.6 Australia

Chapter 11 Historical and Forecast Cystic Fibrosis Therapeutics Market in Europe (2020-2030)
11.1 Cystic Fibrosis Therapeutics Market Size
11.2 Cystic Fibrosis Therapeutics Market by End Use
11.3 Competition by Players/Suppliers
11.4 Cystic Fibrosis Therapeutics Market Size by Type
11.5 Key Countries Analysis
11.5.1 Germany
11.5.2 France
11.5.3 United Kingdom
11.5.4 Italy
11.5.5 Spain
11.5.6 Belgium
11.5.7 Netherlands
11.5.8 Austria
11.5.9 Poland
11.5.10 Russia

Chapter 12 Historical and Forecast Cystic Fibrosis Therapeutics Market in MEA (2020-2030)
12.1 Cystic Fibrosis Therapeutics Market Size
12.2 Cystic Fibrosis Therapeutics Market by End Use
12.3 Competition by Players/Suppliers
12.4 Cystic Fibrosis Therapeutics Market Size by Type
12.5 Key Countries Analysis
12.5.1 Egypt
12.5.2 Israel
12.5.3 South Africa
12.5.4 Gulf Cooperation Council Countries
12.5.5 Turkey

Chapter 13 Summary For Global Cystic Fibrosis Therapeutics Market (2020-2025)
13.1 Cystic Fibrosis Therapeutics Market Size
13.2 Cystic Fibrosis Therapeutics Market by End Use
13.3 Competition by Players/Suppliers
13.4 Cystic Fibrosis Therapeutics Market Size by Type

Chapter 14 Global Cystic Fibrosis Therapeutics Market Forecast (2025-2030)
14.1 Cystic Fibrosis Therapeutics Market Size Forecast
14.2 Cystic Fibrosis Therapeutics Application Forecast
14.3 Competition by Players/Suppliers
14.4 Cystic Fibrosis Therapeutics Type Forecast

Chapter 15 Analysis of Global Key Vendors
15.1 Vertex Pharmaceuticals
15.1.1 Company Profile
15.1.2 Main Business and Cystic Fibrosis Therapeutics Information
15.1.3 SWOT Analysis of Vertex Pharmaceuticals
15.1.4 Vertex Pharmaceuticals Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.2 AbbVie
15.2.1 Company Profile
15.2.2 Main Business and Cystic Fibrosis Therapeutics Information
15.2.3 SWOT Analysis of AbbVie
15.2.4 AbbVie Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.3 Gilead
15.3.1 Company Profile
15.3.2 Main Business and Cystic Fibrosis Therapeutics Information
15.3.3 SWOT Analysis of Gilead
15.3.4 Gilead Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.4 Roche
15.4.1 Company Profile
15.4.2 Main Business and Cystic Fibrosis Therapeutics Information
15.4.3 SWOT Analysis of Roche
15.4.4 Roche Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.5 Alcresta Therapeutics
15.5.1 Company Profile
15.5.2 Main Business and Cystic Fibrosis Therapeutics Information
15.5.3 SWOT Analysis of Alcresta Therapeutics
15.5.4 Alcresta Therapeutics Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.6 Chiesi Farmaceutici
15.6.1 Company Profile
15.6.2 Main Business and Cystic Fibrosis Therapeutics Information
15.6.3 SWOT Analysis of Chiesi Farmaceutici
15.6.4 Chiesi Farmaceutici Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.7 Merck
15.7.1 Company Profile
15.7.2 Main Business and Cystic Fibrosis Therapeutics Information
15.7.3 SWOT Analysis of Merck
15.7.4 Merck Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
15.8 AstraZeneca
15.8.1 Company Profile
15.8.2 Main Business and Cystic Fibrosis Therapeutics Information
15.8.3 SWOT Analysis of AstraZeneca
15.8.4 AstraZeneca Cystic Fibrosis Therapeutics Revenue, Gross Margin and Market Share (2020-2025)
Please ask for sample pages for full companies list

Tables and Figures
Table Abbreviation and Acronyms
Table Research Scope of Cystic Fibrosis Therapeutics Report
Table Data Sources of Cystic Fibrosis Therapeutics Report
Table Major Assumptions of Cystic Fibrosis Therapeutics Report
Figure Market Size Estimated Method
Figure Major Forecasting Factors
Figure Cystic Fibrosis Therapeutics Picture
Table Cystic Fibrosis Therapeutics Classification
Table Cystic Fibrosis Therapeutics Applications
Table Drivers of Cystic Fibrosis Therapeutics Market
Table Restraints of Cystic Fibrosis Therapeutics Market
Table Opportunities of Cystic Fibrosis Therapeutics Market
Table Threats of Cystic Fibrosis Therapeutics Market
Table Covid-19 Impact For Cystic Fibrosis Therapeutics Market
Table Raw Materials Suppliers
Table Different Production Methods of Cystic Fibrosis Therapeutics
Table Cost Structure Analysis of Cystic Fibrosis Therapeutics
Table Key End Users
Table Latest News of Cystic Fibrosis Therapeutics Market
Table Merger and Acquisition
Table Planned/Future Project of Cystic Fibrosis Therapeutics Market
Table Policy of Cystic Fibrosis Therapeutics Market
Table 2020-2030 North America Cystic Fibrosis Therapeutics Market Size
Figure 2020-2030 North America Cystic Fibrosis Therapeutics Market Size and CAGR
Table 2020-2030 North America Cystic Fibrosis Therapeutics Market Size by Application
Table 2020-2025 North America Cystic Fibrosis Therapeutics Key Players Revenue
Table 2020-2025 North America Cystic Fibrosis Therapeutics Key Players Market Share
Table 2020-2030 North America Cystic Fibrosis Therapeutics Market Size by Type
Table 2020-2030 United States Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Canada Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Mexico Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 South America Cystic Fibrosis Therapeutics Market Size
Figure 2020-2030 South America Cystic Fibrosis Therapeutics Market Size and CAGR
Table 2020-2030 South America Cystic Fibrosis Therapeutics Market Size by Application
Table 2020-2025 South America Cystic Fibrosis Therapeutics Key Players Revenue
Table 2020-2025 South America Cystic Fibrosis Therapeutics Key Players Market Share
Table 2020-2030 South America Cystic Fibrosis Therapeutics Market Size by Type
Table 2020-2030 Brazil Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Argentina Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Chile Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Peru Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Asia & Pacific Cystic Fibrosis Therapeutics Market Size
Figure 2020-2030 Asia & Pacific Cystic Fibrosis Therapeutics Market Size and CAGR
Table 2020-2030 Asia & Pacific Cystic Fibrosis Therapeutics Market Size by Application
Table 2020-2025 Asia & Pacific Cystic Fibrosis Therapeutics Key Players Revenue
Table 2020-2025 Asia & Pacific Cystic Fibrosis Therapeutics Key Players Market Share
Table 2020-2030 Asia & Pacific Cystic Fibrosis Therapeutics Market Size by Type
Table 2020-2030 China Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 India Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Japan Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 South Korea Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Southeast Asia Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Australia Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Europe Cystic Fibrosis Therapeutics Market Size
Figure 2020-2030 Europe Cystic Fibrosis Therapeutics Market Size and CAGR
Table 2020-2030 Europe Cystic Fibrosis Therapeutics Market Size by Application
Table 2020-2025 Europe Cystic Fibrosis Therapeutics Key Players Revenue
Table 2020-2025 Europe Cystic Fibrosis Therapeutics Key Players Market Share
Table 2020-2030 Europe Cystic Fibrosis Therapeutics Market Size by Type
Table 2020-2030 Germany Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 France Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 United Kingdom Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Italy Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Spain Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Belgium Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Netherlands Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Austria Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Poland Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Russia Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 MEA Cystic Fibrosis Therapeutics Market Size
Figure 2020-2030 MEA Cystic Fibrosis Therapeutics Market Size and CAGR
Table 2020-2030 MEA Cystic Fibrosis Therapeutics Market Size by Application
Table 2020-2025 MEA Cystic Fibrosis Therapeutics Key Players Revenue
Table 2020-2025 MEA Cystic Fibrosis Therapeutics Key Players Market Share
Table 2020-2030 MEA Cystic Fibrosis Therapeutics Market Size by Type
Table 2020-2030 Egypt Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Israel Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 South Africa Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Gulf Cooperation Council Countries Cystic Fibrosis Therapeutics Market Size
Table 2020-2030 Turkey Cystic Fibrosis Therapeutics Market Size
Table 2020-2025 Global Cystic Fibrosis Therapeutics Market Size by Region
Table 2020-2025 Global Cystic Fibrosis Therapeutics Market Size Share by Region
Table 2020-2025 Global Cystic Fibrosis Therapeutics Market Size by Application
Table 2020-2025 Global Cystic Fibrosis Therapeutics Market Share by Application
Table 2020-2025 Global Cystic Fibrosis Therapeutics Key Vendors Revenue
Figure 2020-2025 Global Cystic Fibrosis Therapeutics Market Size and Growth Rate
Table 2020-2025 Global Cystic Fibrosis Therapeutics Key Vendors Market Share
Table 2020-2025 Global Cystic Fibrosis Therapeutics Market Size by Type
Table 2020-2025 Global Cystic Fibrosis Therapeutics Market Share by Type
Table 2025-2030 Global Cystic Fibrosis Therapeutics Market Size by Region
Table 2025-2030 Global Cystic Fibrosis Therapeutics Market Size Share by Region
Table 2025-2030 Global Cystic Fibrosis Therapeutics Market Size by Application
Table 2025-2030 Global Cystic Fibrosis Therapeutics Market Share by Application
Table 2025-2030 Global Cystic Fibrosis Therapeutics Key Vendors Revenue
Figure 2025-2030 Global Cystic Fibrosis Therapeutics Market Size and Growth Rate
Table 2025-2030 Global Cystic Fibrosis Therapeutics Key Vendors Market Share
Table 2025-2030 Global Cystic Fibrosis Therapeutics Market Size by Type
Table 2025-2030 Cystic Fibrosis Therapeutics Global Market Share by Type

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